Gene index

2 article(s) in the watch · Constitutional genetics

FGF14 modulates neuronal excitability. An intronic GAA repeat expansion causes spinocerebellar ataxia type 27B, a common late-onset ataxia; point variants cause SCA27A.

InheritanceAutosomal dominant
Clinical spectrumLate-onset cerebellar ataxia (SCA27B), early-onset forms (SCA27A)
ManagementTargeted GAA-expansion testing; 4-aminopyridine benefits some patients.

Curated publications